About Sickle Cell Disease
Sickle Cell Disease (SCD), hemophilia, and some other blood disorders are severe, lifelong, and presently incurable diseases. We are instituting new programs to study and better treat iron overload in multiply transfused patients, comprehensive management of cardiac and pulmonary disease in SCD, and other initiatives to improve the transition of care from adolescence to adulthood and overall quality of life of these patients. The University of Florida is at the forefront of research in AAV (adeno-associated virus) vectors for gene therapy that aims to cure SCD and hemophilia while promising to cure other similar illnesses caused by single gene defects.
- State Newborn Testing
- Sickle Cell Trait
- Sickle Cell Complications
- Chronic Transfusion Therapy
- Sickle Cell Awareness 2K Walk
Safe vectors for gene therapy for Sickle Cell Anemia and other blood disorders.
Developmental regulation of the human globin genes.
Develop gene therapy for the X-linked bleeding disorder hemophilia.